Source: Jastreboff A.M. et al., The New England Journal of Medicine, 2023, 10.1056/NEJMoa2301972
Study Objective
To evaluate the efficacy, safety, and dose-response effect of Retatrutide – a triple GIP, GLP-1, and glucagon receptor agonist – in adults with overweight and obesity. Retatrutide is a peptide agonist with an extended half-life (~6 days), allowing for weekly subcutaneous administration. The study aims to determine the degree of weight reduction and the frequency of adverse events at different doses.
Study Design
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Type: Phase 2, double-blind, randomized, placebo-controlled study
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Participants: 338 adults (BMI ≥30 or BMI ≥27 with a coexisting condition)
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Groups: Retatrutide 1 mg, 4 mg, 8 mg, 12 mg (different initial doses – 2 or 4 mg) and placebo
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Duration: 48 weeks (plus 4 weeks follow-up)
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Administration: subcutaneous, 1x weekly
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Primary endpoint: percentage change in body weight at week 24
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Secondary endpoints: change in weight at week 48, ≥5%, ≥10%, ≥15% weight reduction; safety and tolerability
Key Results
Weight Reduction
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Mean percentage change in weight at week 48:
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1 mg: −8.7%
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4 mg: −17.1%
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8 mg: −22.8%
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12 mg: −24.2%
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Placebo: −2.1%
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100% of participants on 8 mg and 12 mg achieved ≥5% reduction; 91–93% achieved ≥10%; 75–83% achieved ≥15%
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26% of participants on 12 mg achieved ≥30% weight reduction
Cardiometabolic Parameters
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Improvements in blood pressure, HbA1c, fasting glucose, insulin, LDL-cholesterol
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72% of patients with prediabetes achieved normoglycemia
Safety
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Most common adverse events: gastrointestinal (nausea, diarrhea, constipation), dose-dependent, predominantly mild to moderate
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Heart rate: slight increase up to week 24, then decrease
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No severe hypoglycemia, medullary carcinoma, or C-cell hyperplasia
Conclusions
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Retatrutide induced significant, dose-dependent weight reduction of up to −24.2% over 48 weeks.
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Improved cardiometabolic profile and glycemic control.
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Adverse events were similar to those with GLP-1 and GIP-GLP-1 agonists.
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Suitable for further studies (Phase 3) in patients with obesity.
Limitations
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Duration – 48 weeks (lack of long-term data)
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Predominantly white population from the USA – limited generalizability
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Small proportion of participants with BMI <30
Practical Implications
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Retatrutide is a potent triple GIP/GLP-1/glucagon receptor agonist with the potential to achieve weight reduction comparable to bariatric surgery.
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A promising therapy for investigation in obesity without type 2 diabetes.